Publication & Citation Trends
Most Cited Works
Publications
115 total
Gene Editing for Haemophilia—The Next Frontier
Cited by 0
Semantic Scholar
Modulating Collagen I Expression in Fibroblasts by CRISPR-Cas9 Base Editing of the Collagen 1A1 Promoter OA
Cited by 6
Semantic Scholar
Author Correction: In vivo base editing extends lifespan of a humanized mouse model of prion disease
Cited by 0
Semantic Scholar
Base editing of trinucleotide repeats that cause Huntington’s disease and Friedreich’s ataxia reduces somatic repeat expansions in patient cells and in mice
Cited by 19
Semantic Scholar
FLT1 and other candidate fetal haemoglobin modifying loci in sickle cell disease in African ancestries OA
Cited by 5
Semantic Scholar
Comparative Analysis of CRISPR-Cas9, Lentiviral Transduction, and Base Editing for Sickle Cell Disease Therapy in a Murine Model
Cited by 0
Semantic Scholar
Mitochondrial DNA copy number reduction via in vitro TFAM knockout remodels the nuclear epigenome and transcriptome
Cited by 0
Semantic Scholar
Abstract 4370250: Regulatory Profiling of LMNA Identifies Therapeutic Targets for LMNA-Associated Dilated Cardiomyopathy
Cited by 0
Semantic Scholar
Research Topics
CRISPR and Genetic Engineering
(76)
Virus-based gene therapy research
(22)
RNA regulation and disease
(22)
RNA and protein synthesis mechanisms
(19)
Advanced biosensing and bioanalysis techniques
(15)
Frequent Co-Authors
Affiliations
Broad Institute
Howard Hughes Medical Institute
Harvard University
Johns Hopkins University
Elon University