Nicole M. Gaudelli
0000-0001-8608-4855
Publication & Citation Trends
Publications
31 total
Engineered Stem Cell Antibody Paired Evasion 1 (ESCAPE-1): Paired HSC Epitope Engineering and Upregulation of Fetal Hemoglobin for Antibody-Mediated Autologous Hematopoietic Stem Cell Therapy Conditioning for the Treatment of Hemoglobinopathies OA
Cited by 1
Semantic Scholar
Engineered Stem Cell Antibody Paired Evasion-2 (ESCAPE-2): Paired HSC Epitope Engineering and Direct Editing of Sickle Allele for Antibody-Mediated Autologous Hematopoietic Stem Cell Therapy Conditioning for the Treatment of Sickle Cell Disease OA
Cited by 1
Semantic Scholar
Rationally Designed Base Editors for Precise Editing of the Sickle Cell Disease Mutation
Cited by 67
Semantic Scholar
Engineering Cas9 for human genome editing.
Cited by 28
Semantic Scholar
CRISPR-derived genome editing therapies: progress from bench to bedside. OA
Cited by 14
Semantic Scholar
Conversion of HbS to Hb G-Makassar By Adenine Base Editing Is Compatible with Normal Hemoglobin Function OA
Cited by 19
Semantic Scholar
Research Topics
CRISPR and Genetic Engineering
(19)
Microbial Natural Products and Biosynthesis
(5)
Virus-based gene therapy research
(5)
RNA and protein synthesis mechanisms
(4)
RNA regulation and disease
(4)
Affiliations
Broad Institute
Howard Hughes Medical Institute
Harvard University
Johns Hopkins University
Beam Engineering for Advanced Measurements (United States)