Publication & Citation Trends
Publications
0 total
No publications found.
Research Topics
Lysosomal Storage Disorders Research
(185)
Virus-based gene therapy research
(137)
Glycogen Storage Diseases and Myoclonus
(114)
Neurogenetic and Muscular Disorders Research
(58)
Muscle Physiology and Disorders
(52)
Affiliations
University College Dublin
Cedars-Sinai Medical Center
Cincinnati Children's Hospital Medical Center
Boston Children's Hospital
National Institutes of Health