Publication & Citation Trends
Publications
0 total
No publications found.
Research Topics
Virus-based gene therapy research
(63)
Genetics and Neurodevelopmental Disorders
(52)
Metabolism and Genetic Disorders
(48)
Genomics and Rare Diseases
(43)
Genomic variations and chromosomal abnormalities
(33)
Affiliations
Beth Israel Deaconess Medical Center
University of Salerno
Howard Hughes Medical Institute
Inserm
Baylor College of Medicine