Publication & Citation Trends
Publications
29 total
Base-editing corrects metabolic abnormalities in a humanized mouse model for glycogen storage disease type-Ia PDF
Cited by 11
OpenAlex
Base-editing corrects metabolic abnormalities in a humanized mouse model for glycogen storage disease type-Ia PDF
Cited by 0
OpenAlex
Cytosine base editing inhibits hepatitis B virus replication and reduces HBsAg expression in vitro and in vivo PDF
Cited by 31
OpenAlex
Phage-Assisted Evolution of Botulinum Neurotoxin Proteases With Reprogrammed Specificity
Cited by 2
OpenAlex
Conversion of HbS to Hb G-Makassar By Adenine Base Editing Is Compatible with Normal Hemoglobin Function
Cited by 21
OpenAlex
Adenine Base Editing of the Sickle Allele in CD34+ Hematopoietic Stem and Progenitor Cells Eliminates Hemoglobin S
Cited by 2
OpenAlex
Complementary Base Editing Approaches for the Treatment of Sickle Cell Disease and Beta Thalassemia
Cited by 8
OpenAlex
Research Topics
CRISPR and Genetic Engineering
(15)
RNA and protein synthesis mechanisms
(5)
Virus-based gene therapy research
(5)
Botulinum Toxin and Related Neurological Disorders
(4)
Hemoglobinopathies and Related Disorders
(3)
Affiliations
Broad Institute
Howard Hughes Medical Institute
Harvard University
Cornell University
Beam Therapeutics (United States)