Publication & Citation Trends
Publications
0 total
No publications found.
Research Topics
Lysosomal Storage Disorders Research
(23)
Virus-based gene therapy research
(13)
Neurogenetic and Muscular Disorders Research
(12)
RNA modifications and cancer
(8)
Muscle Physiology and Disorders
(7)
Affiliations
State University of New York
Children's Hospital of Philadelphia
Sanofi (France)
California University of Pennsylvania
Ospedale Maggiore