Publication & Citation Trends
Most Cited Works
Publications
75 total
Base editing of β0 thalassemia mutations as a therapeutic strategy for β-hemoglobinopathies: efficacy and genotoxicity studies
Cited by 0
Semantic Scholar
Decoding the role of inflammatory signaling in shaping HSC heterogeneity and engraftment in gene therapy-treated β-thalassemia pediatric patients
Cited by 0
Semantic Scholar
Acute Myeloid Leukemia eradication targeting cathepsin g with a dual HLA-restricted TCR
Cited by 0
Semantic Scholar
Base editing of β0-thalassemia mutations as a therapeutic strategy for severe β-hemoglobinopathies.
Cited by 1
Semantic Scholar
Imbalanced TGFβ signalling and autophagy drive erythroid priming of hematopoietic stem cells in β-thalassemia
Cited by 1
Semantic Scholar
3050 – UNIQUE TNFΑ-NFKB SIGNALING DYNAMICS REGULATES HEMATOPOIETIC STEM CELL LINEAGE FATE IN BETA-THALASSEMIA
Cited by 0
Semantic Scholar
3117 – HSCS IN Β-THALASSEMIA HAVE A REDUCED DORMANCY AND AN ERYTHROID BIASED LINEAGE COMMITMENT IN RESPONSE TO ALTERED TGFΒ SIGNALING IN THE BM MICROENVIRONMENT
Cited by 0
Semantic Scholar
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies. OA
Cited by 14
Semantic Scholar
Gene Therapy for Hemoglobinopathies
Cited by 5
Semantic Scholar
Research Topics
Virus-based gene therapy research
(34)
CAR-T cell therapy research
(26)
CRISPR and Genetic Engineering
(21)
Hemoglobinopathies and Related Disorders
(14)
RNA Interference and Gene Delivery
(11)
Frequent Co-Authors
Affiliations
Humanitas University
Vita-Salute San Raffaele University
Rigshospitalet
San Raffaele University of Rome
Institute of Genetic and Biomedical Research